Gene Therapy Halts Brain Disease in Two Boys

Researchers have used a modified AIDS virus to halt a devastating brain disease in two young boys. The treatment, in which the virus delivered a therapeutic gene, marks the first time gene therapy has been successfully used against X-linked adrenoleukodystrophy (ALD)–a disorder that is always fatal if untreated. With this proof of principle, scientists hope versions of the AIDS virus engineered to carry different genes can now be applied to a variety of other diseases.

via Gene Therapy Halts Brain Disease in Two Boys — Kaiser 2009 (1105): 1 — ScienceNOW.

Advertisements

One thought on “Gene Therapy Halts Brain Disease in Two Boys

  1. The use of viruses to deliver gene therapy or to deliver drugs is a very promising area of disease treatment. As the approaches mature, it will be interesting to see whether nanoparticles or viruses become the predominant means for accomplishing such tasks.

Leave a Reply

Fill in your details below or click an icon to log in:

WordPress.com Logo

You are commenting using your WordPress.com account. Log Out / Change )

Twitter picture

You are commenting using your Twitter account. Log Out / Change )

Facebook photo

You are commenting using your Facebook account. Log Out / Change )

Google+ photo

You are commenting using your Google+ account. Log Out / Change )

Connecting to %s